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List of Treatments for Muscular Dystrophy

See what members are saying about muscular dystrophy treatments, the side effects to expect, and the drug basics.

All treatment information is medically reviewed · February 17, 2026

Agamree (Vamorolone)

Overview
Agamree is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people ages 2 years and older. It is prescribed for managing symptoms associated with DMD, a…

Amondys 45 (Casimersen)

Overview
Amondys 45 is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) in the DMD gene that is responsive to exon 45…

Duvyzat (Givinostat)

Overview
Duvyzat is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people who are 6 years of age and older. A person must undergo evaluations of their platelet…

Elevidys (Delandistrogene Moxeparvovec-Rokl)

Overview

Elevidys is approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in children aged 4 years and older who are ambulatory (still able to walk) and have a…

Emflaza (Deflazacort)

Overview
Emflaza is approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people 2 years of age and older. It is specifically indicated for use in children and…

Exondys 51 (Eteplirsen)

Overview
Exondys 51 is approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) of the DMD gene that allows for exon 51…

Jaythari (Deflazacort) for Muscular Dystrophy

Overview
Jaythari is a corticosteroid medication approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people 5 years of age and older. To be eligible for…

Pyquvi (Deflazacort) for Muscular Dystrophy

Overview
Pyquvi is a corticosteroid medication approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people 5 years of age and older. Pyquvi is also known by its…

Viltepso (Viltolarsen)

Overview
Viltepso is approved by the U.S. Food and Drug Administration (FDA) under accelerated approval for treating Duchenne muscular dystrophy (DMD) in people with a specific mutation (variation) in the DMD gene that is…

Vyondys 53 (Golodirsen)

Overview
Vyondys 53, approved by the U.S. Food and Drug Administration (FDA), is used to treat Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) of the DMD gene that allows for exon 53…

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