List of Treatments for Muscular Dystrophy

Below is a listing of treatments and therapies for muscular dystrophy. Click on one to read more information or connect with others currently using it.

Agamree (Vamorolone)

Overview
Agamree is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people ages 2 years and older. It is prescribed for managing symptoms associated with DMD, a…

Amondys 45 (Casimersen)

Overview
Amondys 45 is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) in the DMD gene that is responsive to exon 45…

Duvyzat (Givinostat)

Overview
Duvyzat is approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people who are 6 years of age and older. A person must undergo evaluations of their platelet…

Elevidys (Delandistrogene Moxeparvovec-Rokl)

Overview
Elevidys is a gene therapy approved by the U.S. Food and Drug Administration (FDA) for treating Duchenne muscular dystrophy (DMD) in people 4 years or older with a confirmed DMD gene mutation (variation). To be…

Emflaza (Deflazacort)

Overview
Emflaza is approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people 2 years of age and older. It is specifically indicated for use in children and…

Exondys 51 (Eteplirsen)

Overview
Exondys 51 is approved by the U.S. Food and Drug Administration (FDA) for the treatment of Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) of the DMD gene that allows for exon 51…

Prednisone

Overview
Prednisone is a corticosteroid approved by the U.S. Food and Drug Administration (FDA) for treating inflammatory and immune-related conditions such as arthritis, lupus, and certain cancers. It is also used…

Viltepso (Viltolarsen)

Overview
Viltepso is approved by the U.S. Food and Drug Administration (FDA) under accelerated approval for treating Duchenne muscular dystrophy (DMD) in people with a specific mutation (variation) in the DMD gene that is…

Vyondys 53 (Golodirsen)

Overview
Vyondys 53, approved by the U.S. Food and Drug Administration (FDA), is used to treat Duchenne muscular dystrophy (DMD) in people with a confirmed mutation (variation) of the DMD gene that allows for exon 53…

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